Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
Conditions
Duchenne Muscular Dystrophy
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Queen Fabiola Children's University Hospital HUDERF, Brussels, Belgium
Contact: Study coordinator (Nicolas Deconinck, MD) · nicolas.deconink@hubruxelles.be · +32 2 4772945Fondazione Serena Onlus - Azienda Ospedaliera Niguarda Ca' Granda - NeuroMuscolar Omnicenter, Milan, Italy
Ospedale Pediatrico Bambino Gesù, Roma, Italy
Policlinico Universitario Agostino Gemelli - Università Cattolica del Sacro Cuore, Roma, Italy
Contact: Study coordinator (Eugenio Mercuri, MD) · eugeniomaria.mercuri@policlinicogemelli.it · +39 06 30158576Leids Universitair Medisch Centrum (LUMC), Leiden, Netherlands
Leeds Teaching Hospital NHS Trust, Leeds, England, United Kingdom
Great Ormond Street Hospital - GOSH, London, England, United Kingdom
Contact: Study coordinator (Mariacristina Scoto, MD) · Mariacristina Scoto <Mariacristina.Scoto@gosh.nhs.uk>Newcastle upon Tyne Hospitals NHS Foundation Trust - Newcastle University, Newcastle upon Tyne, England, United Kingdom
Contact: Study coordinator (Michela Guglieri, MD) · Michela Guglieri <michela.guglieri@newcastle.ac.uk>Oxford University Hospitals NHS Foundation Trust, Oxford, England, United Kingdom
Contact: Study coordinator (Laurent Servais, MD) · Laurent Servais <laurent.servais@paediatrics.ox.ac.uk>