Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Conditions
Duchenne Muscular Dystrophy
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Locations
Universitaire Ziekenhuizen Leuven, Leuven, Belgium
Contact: Principal Investigator (Liesbeth De Waele, MD)British Columbia Children's Hospital, Vancouver, British Columbia, Canada
Contact: Principal Investigator (Kathryn Selby, MD)The University of Western Ontario - Children's Health Research Institute, London, Ontario, Canada
Contact: Principal Investigator (Craig Campbell, MD)University of Ottawa - Children's Hospital of Eastern Ontario, Ottawa, Ontario, Canada
Contact: Principal Investigator (Hugh McMillan, MD)University of Toronto - Holland Bloorview Kids Rehabilitation Hospital, Toronto, Ontario, Canada
Contact: Principal Investigator (Laura McAdam, MD)Klinika dětské neurologie 2. LF, Fakultní nemocnice v Motole, Prague, Czechia
Centre Hospitalier Régional Universitaire de Lille, Lille, France
Contact: Principal Investigator (Jean-Baptiste Davion, MD)Centre hospitalier universitaire - Hôpitaux de Marseille, Marseille, France
Contact: Principal Investigator (Cecile Halbert, MD)Hôpital Armand-Trousseau - I-Motion, Paris, France
Contact: Principal Investigator (Marina Colella, MD)Charite-Universitaetsmedizin Berlin, Berlin, Germany
Contact: Principal Investigator (Joanna Schneider, MD)Universitätsklinikum Essen Kinder-und Jugendmedizin Neuropadiatrie, Essen, Germany
Universitaetsklinikum Freiburg, Freiburg im Breisgau, Germany
Contact: Principal Investigator (Janbernd Kirschner, MD)Universitätsklinikum Hamburg-Eppendorf, Klinik und Poliklinik für Kinder- und Jugendmedizin, Hamburg, Germany
Associazione La Nostra Famiglia - IRCCS Eugenio Medea - Bosisio Parini, Lecco, Italy
Contact: Principal Investigator (Maria Grazia D´Angelo, MD)Fondazione Serena Onlus - Azienda Ospedaliera Niguarda Ca' Granda - NeuroMuscular Omnicentre, Milan, Italy
Contact: Principal Investigator (Valeria Sansone, MD)Università degli Studi di Padova - Azienda Ospedaliera di Padova, Padova, Italy
Contact: Principal Investigator (Elena Pegoraro, MD)Ospedale Pediatrico Bambino Gesù, Roma, Italy
Contact: Principal Investigator (Adele D´Amico, MD)Policlinico Universitario Agostino Gemelli - Università Cattolica del Sacro Cuore, Roma, Italy
Contact: Principal Investigator (Eugenio M Mercuri, MD)Leids Universitair Medisch Centrum (LUMC), Leiden, Netherlands
Contact: Principal Investigator (Erik Niks, MD)Radboud Universitair Medisch Centrum (Radboudumc), Nijmegen, Netherlands
Contact: Principal Investigator (Saskia Houwen-van Opstal, MD)Uniwersyteckie Centrum Kliniczne, Klinika Neurologii Rozwojowej, Gdansk, Poland
Uniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny, Warsaw, Poland
Clinic of Neurology and Psychiatry for Children and Youth, Belgrade, Serbia
Hospital Sant Joan de Déu, Barcelona, Spain
Hospital Universitario y Politécnico La Fe, Valencia, Spain
Karolinska University Hospital, Solna CKB Centrum för Kliniska Barnstudier, Stockholm, Sweden
Newcastle upon Tyne Hospitals NHS Foundation Trust - Newcastle University, Newcastle upon Tyne, England, United Kingdom
Oxford University Hospitals NHS Foundation Trust, Oxford, England, United Kingdom
NHS Greater Glasgow and Clyde - Royal Hospital for Children, Glasgow, Scotland, United Kingdom