A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy
Conditions
Duchenne Muscular Dystrophy
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Locations
Republican Scientific and Practical Center Mother and Child, Minsk, Belarus
Contact: Principal Investigator (Irina V. Zhevneronok, Ph.D.)Russian Children's Clinical Hospital, Moscow, Russia
Contact: Principal Investigator (Svetlana V. Mikhailova, Dr. Med. Sci.)National Medical Research Center for Children, Moscow, Russia
Contact: Principal Investigator (Lyudmila M. Kuzenkova, Dr. Med. Sci., professor)Veltischev Research and Clinical Institute for Pediatrics and Pediatric Surgery of the Pirogov Russian National Research Medical University, Moscow, Russia
Contact: Principal Investigator (Dmitry V. Vlodavets, Dr. Med. Sci.)Saint Petersburg State Pediatric Medical University, Saint Petersburg, Russia
Contact: Principal Investigator (Vasily M. Suslov, Ph.D.)Regional Children's Clinical Hospital, Yekaterinburg, Russia
Contact: Principal Investigator (Olga A. Lvova, Dr. Med. Sci.)
Study leads
Oksana A. Markova, M.D.
Study Chair
AO GENERIUM