A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Conditions
Duchenne Muscular Dystrophy
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Aravindhan Veerapandiyan, MD)University of California, Los Angeles Medical Center, Los Angeles, California, United States
Contact: Principal Investigator (Perry Shieh, MD, PhD)University of California, Davis, Sacramento, California, United States
Contact: Principal Investigator (Craig McDonald, MD)University of California, San Diego, California, United States
Contact: Principal Investigator (Chamindra Laverty, MD)Rare Disease Research, Atlanta, Georgia, United States
Contact: Principal Investigator (Renata Shih, MD)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Study coordinator (Nancy Kuntz, MD)Washington University in St. Louis, St Louis, Missouri, United States
Contact: Study coordinator (Natalie Goedeker) · neuromusclepediatricresearch@wustl.edu · 314-362-4919Contact: Principal Investigator (Craig Zaidman, MD)Nationwide Children's Hospital, Columbus, Ohio, United States
Contact: Principal Investigator (Kevin Flanigan, MD)Oregon Health and Sciences University, Portland, Oregon, United States
Contact: Principal Investigator (Erika Finanger, MD)Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (John Brandsema, MD)Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud, MD)Seattle Children's Hospital, Seattle, Washington, United States
Contact: Principal Investigator (Alicia Henriquez, MD)The Hospital for Sick Children, Toronto, Ontario, Canada
Contact: Principal Investigator (Hernan Gonorazky, MD)Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy
Contact: Study coordinator (Lorenzo Stivala) · lorenzo.stivala@policlinicogemelli.it · +39 063-015-6330Contact: Principal Investigator (Eugenio Mercuri, MD, PhD)Great Ormond Street Hospital, London, United Kingdom
Contact: Principal Investigator (Francesco Muntoni, MD)
Study leads
Solid Bio Clinical Trials
Study Director
Solid Biosciences