Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)
Conditions
Duchenne Muscular Dystrophy
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Aravindhan Veerapandiyan, Dr)Rare Disease Research LLC, Atlanta, Georgia, United States
Contact: Study coordinator (Scott Batchelor, Dr) · sbatchelor@rarediseaseresearch.com · 404-782-8239Contact: Principal Investigator (Scott Batchelor, Dr)Istiklal Hospital/ Clinical Research Unit, Amman, Jordan
Contact: Principal Investigator (Muath Alqurashi, Dr)The Specialty Hospital (TSH)/ Advanced Clinical Center, Amman, Jordan
Contact: Principal Investigator (Mai Bader, Dr)Oxford Children's Hospital, Oxford University Hospitals NHS Foundation Trust, Headington, Oxford, United Kingdom
Contact: Principal Investigator (Laurent Servais, MD, PhD)
Study leads
Medical Director, MD
Study Director
Wave Life Sciences