Finding the Optimum Regimen for Duchenne Muscular Dystrophy

Abroad (travel likely)CompletedPHASE3

Conditions

Duchenne Muscular Dystrophy

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • University of California Los Angeles (UCLA) Medical Center, Los Angeles, California, United States

  • University of California Davis Medical Center, Sacramento, California, United States

  • Children's National Medical Center, Washington D.C., District of Columbia, United States

  • Nemours Children's Hospital, Orlando, Florida, United States

  • Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

  • University of Kansas Medical Center, Kansas City, Kansas, United States

  • Boston Children's Hospital, Boston, Massachusetts, United States

  • University of New Mexico Health Science Center, Albuquerque, New Mexico, United States

  • University of Rochester Medical Center, Rochester, New York, United States

  • University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, United States

  • Nationwide Children's Hospital, Columbus, Ohio, United States

  • Penn State Hershey Medical Center, Hershey, Pennsylvania, United States

  • Vanderbilt Children's Hospital, Nashville, Tennessee, United States

  • University of Utah Medical Center, Salt Lake City, Utah, United States

  • Alberta Children's Hospital, Calgary, Alberta, Canada

  • Children's Hospital London Health Sciences Centre, London, Ontario, Canada

  • Children's Hospital of Eastern Ontario (CHEO), Ottawa, Ontario, Canada

  • Children's Hospital, Technical University Dresden, Dresden, Germany

  • University Hospital of Essen, Essen, Germany

  • University Medical Center Freiburg, Freiburg im Breisgau, Germany

  • Children's University Hospital, Göttingen, Göttingen, Germany

  • University of Messina AOU Policlinico Gaetano Martino, Messina, Italy

  • C. Besta Neurological Institute Foundation, Milan, Italy

  • University of Padova School of Medicine, Padova, Italy

  • Neuromuscular Center University of Turin, Torino, Italy

  • The General Infirmary at Leeds, Leeds, England, United Kingdom

  • Greater Glasgow and Clyde NHS Yorkhill Hospital, Glasgow, Scotland, United Kingdom

  • Heart of England NHS Foundation Trust Birmingham Heartland's Hospital, Birmingham, United Kingdom

  • Alder Hey Children's Hospital NHS Trust, Liverpool, United Kingdom

  • Great Ormond Street Hospital for Children NHS Trust, London, United Kingdom

  • Royal Manchester Children's Hospital, Manchester, United Kingdom

  • Institute of Human Genetics, International Centre for Life, Newcastle upon Tyne, United Kingdom

Study leads
  • Robert C. Griggs, MD

    Principal Investigator

    University of Rochester

  • Kate Bushby, MD

    Principal Investigator

    Newcastle University