AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
Conditions
Duchenne Muscular Dystrophy
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This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Aravindhan Veerapandiyan, MD)Stanford School of Medicine /Division of Neuromuscular Medicine, Palo Alto, California, United States
Contact: Principal Investigator (Carolina Tesi-Rocha, MD)Children's Hospital Colorado, Aurora, Colorado, United States
Contact: Principal Investigator (Michele Yang, MD)University of Florida, Gainesville, Florida, United States
Contact: Principal Investigator (Barry Byrne, MD)Rare Disease Research, Atlanta, Georgia, United States
Contact: Study coordinator (Maureen Ikpeoha) · maureen.ikpeoha@rarediseaseresearch.com · 470-666-1884Contact: Principal Investigator (Han Phan, MD)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Nancy L Kuntz, MD)University of Iowa, Iowa City, Iowa, United States
Contact: Principal Investigator (Dimah Saade, MD)University of Massachusetts Chan Medical School, Worcester, Massachusetts, United States
Contact: Principal Investigator (Eleonora D'Ambrosio, MD)Cincinnati Children's, Cincinnati, Ohio, United States
Contact: Principal Investigator (Cuixia Tian, MD)Oregon Health & Science University, Portland, Oregon, United States
Contact: Principal Investigator (Erika Finanger, MD)The University of Texas Southwestern Medical Center, Dallas, Texas, United States
Contact: Principal Investigator (Susan Iannaccone, MD)Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud, MD)Children's Hospital of Richmond at Virginia Commonwealth University, Richmond, Virginia, United States
Contact: Principal Investigator (Amy Harper, MD)Alberta Children's Hospital, Calgary, Alberta, Canada
Contact: Principal Investigator (Jean Mah, MD)BC Children's Hospital, Vancouver, British Columbia, Canada
Contact: Principal Investigator (Kathryn Selby, MD)Children's Hospital London Health Science Centre, London, Ontario, Canada
Contact: Principal Investigator (Craig Campbell, MD)Children's Hospital of Eastern Ontario, Ottawa, Ontario, Canada
Contact: Principal Investigator (Hugh McMillan, MD)