Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

Abroad (travel likely)RecruitingPHASE3

Conditions

Duchenne Muscular Dystrophy (DMD) · Muscular Dystrophy, Duchenne · Muscular Dystrophy (DMD) · DMD · Muscular Dystrophies · Muscular Dystrophy in Children · Muscular Dystrophy, Duchenne Type · Muscular Dystrophy, Duchenne and Becker Types · Muscular Dystrophies (Duchenne, Becker, Myotonic Dystrophy) · Genetic Disease, Inborn · Genetic Disease, X-Linked · Congenital, Hereditary, and Neonatal Diseases and Abnormalities · Neuromuscular Diseases (NMD)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

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