A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE2

מצבים רפואיים

Spinal Muscular Atrophy (SMA)

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • Arkansas Children's Hospital, Little Rock, Arkansas, United States

    Contact: Study coordinator (Steven Giompoletti) · giompolettis@archildrens.org · (501) 364-1430
    Contact: Principal Investigator (Kapil Arya, Dr.)
  • Rady Childrens Hospital, San Diego, California, United States

    Contact: Study coordinator (Gabriella Penner) · gpenner@excellresearch.com · (760) 758-2222
    Contact: Principal Investigator (Chamindra Laverty, Dr.)
  • Stanford University Medical Center, Stanford, California, United States

    Contact: Study coordinator (Lidia Choniawko) · lidiacho@stanford.edu · (650) 304-8094
    Contact: Principal Investigator (Carolina Tesi Rocha, Dr.)
  • Connecticut Children's Medical Center, Hartford, Connecticut, United States

    Contact: Study coordinator (Gyula Acsadi) · gacsadi@connecticutchildrens.org · (860) 545-9460
    Contact: Principal Investigator (Gyula Acsadi, Dr.)
  • Rare Disease Research FL LLC, Kissimmee, Florida, United States

    Contact: Study coordinator (Maria Cordero) · maria.cordero@rarediseaseresearch.com · (407) 545-7610
    Contact: Principal Investigator (Renata Shih, Dr.)
  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

    Contact: Study coordinator (Alka Maheshwari) · amaheshwari@luriechildrens.org · (815) 444-6362
    Contact: Principal Investigator (Nancy Kuntz, Dr.)
  • University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States

    Contact: Study coordinator (Katherine Mathews) · katherine-mathews@uiowa.edu · (319) 356-1851
    Contact: Principal Investigator (Katherine Mathews, Dr.)
  • The Johns Hopkins Hospital, Baltimore, Maryland, United States

    Contact: Study coordinator (Jessica Nance) · jnance6@jhmi.edu · (410) 955-4259
    Contact: Principal Investigator (Jessica Nance, Dr.)
  • Boston Children's Hospital, Boston, Massachusetts, United States

    Contact: Study coordinator (Samantha Remis) · samantha.remis@childrens.harvard.edu · (617) 355-2752
    Contact: Principal Investigator (Basil Darras, Dr.)
  • The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia, Missouri, United States

    Contact: Study coordinator (Heather McHatton) · heathermchatton@health.missouri.edu · (573) 882-7619
    Contact: Principal Investigator (William Arnold, Dr.)
  • Columbia University Herbert Irving Comprehensive Cancer Center, New York, New York, United States

    Contact: Study coordinator (Claudia Chiriboga) · cac3@cumc.columbia.edu · (646) 426-3876
    Contact: Principal Investigator (Claudia Chiriboga, Dr.)
  • Rare Disease Research NC, LLC, Hillsborough, North Carolina, United States

    Contact: Study coordinator (Norma Davis) · norma.davis@rarediseaseresearch.com · (470) 665-3051
    Contact: Principal Investigator (Edward Smith, Dr.)
  • Children's Hospital Philadelphia - Neurology, Philadelphia, Pennsylvania, United States

    Contact: Study coordinator (Karen Monono) · mononok@chop.edu · (267) 425-0158
    Contact: Principal Investigator (John Brandsema, Dr.)
  • St. Jude Children's Research Hospital, Memphis, Tennessee, United States

    Contact: Study coordinator (Richard Finkel) · richard.finkel@stjude.org · (610) 772-6871
    Contact: Principal Investigator (Richard Finkel, Dr.)
  • Neurology Rare Disease Center, Flower Mound, Texas, United States

    Contact: Study coordinator (Natalie Gomez) · Natalie.Gomez@Neuromdcenter.com · (972) 999-1011
    Contact: Principal Investigator (Diana Castro, Dr.)
  • Texas Children's Hospital, Houston, Texas, United States

    Contact: Study coordinator (Timothy Lotze) · tlotze@bcm.edu · (832) 822-1779
    Contact: Principal Investigator (Timothy Lotze, Dr.)
  • Childrens Hospital of The Kings Daughters, Norfolk, Virginia, United States

    Contact: Study coordinator (Crystal Proud) · crystal.proud@chkd.org · (757) 668-9920
    Contact: Principal Investigator (Crystal Proud, Dr.)