A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
מצבים רפואיים
Spinal Muscular Atrophy (SMA)
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Kapil Arya, Dr.)Rady Childrens Hospital, San Diego, California, United States
Contact: Principal Investigator (Chamindra Laverty, Dr.)Stanford University Medical Center, Stanford, California, United States
Contact: Principal Investigator (Carolina Tesi Rocha, Dr.)Connecticut Children's Medical Center, Hartford, Connecticut, United States
Contact: Principal Investigator (Gyula Acsadi, Dr.)Rare Disease Research FL LLC, Kissimmee, Florida, United States
Contact: Principal Investigator (Renata Shih, Dr.)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Nancy Kuntz, Dr.)University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States
Contact: Principal Investigator (Katherine Mathews, Dr.)The Johns Hopkins Hospital, Baltimore, Maryland, United States
Contact: Principal Investigator (Jessica Nance, Dr.)Boston Children's Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Basil Darras, Dr.)The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia, Missouri, United States
Contact: Study coordinator (Heather McHatton) · heathermchatton@health.missouri.edu · (573) 882-7619Contact: Principal Investigator (William Arnold, Dr.)Columbia University Herbert Irving Comprehensive Cancer Center, New York, New York, United States
Contact: Principal Investigator (Claudia Chiriboga, Dr.)Rare Disease Research NC, LLC, Hillsborough, North Carolina, United States
Contact: Principal Investigator (Edward Smith, Dr.)Children's Hospital Philadelphia - Neurology, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (John Brandsema, Dr.)St. Jude Children's Research Hospital, Memphis, Tennessee, United States
Contact: Principal Investigator (Richard Finkel, Dr.)Neurology Rare Disease Center, Flower Mound, Texas, United States
Contact: Principal Investigator (Diana Castro, Dr.)Texas Children's Hospital, Houston, Texas, United States
Contact: Principal Investigator (Timothy Lotze, Dr.)Childrens Hospital of The Kings Daughters, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud, Dr.)