Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy (BLUEBELL)

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE1, PHASE2

מצבים רפואיים

Spinal Muscular Atrophy (SMA)

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • 1. State Institution Republican Scientific and Practical Center "Mother and Child", Minsk, Belarus

    Contact: Study coordinator (Irina V Zhevneronok) · irynazhauniaronak@yandex.ru
  • Federal State Autonomous Educational Institution of Higher Education "N.I. Pirogov Russian National Research Medical University", Ministry of Health of the Russian Federation, Moscow, Russia

    Contact: Study coordinator (Dmitry Vlodavets) · mityaus@gmail.com
  • Federal State Autonomous Educational Institution of Higher Education "N.I. Pirogov Russian National Research Medical University", Ministry of Health of the Russian Federation, Moscow, Russia

    Contact: Study coordinator (Svetlana Mikhailova) · svetychvital@mail.ru
  • Federal State Autonomous Institution "National Medical Research Center for Children's Health", Ministry of Health of the Russian Federation, Moscow, Russia

    Contact: Study coordinator (Ludmila Kuzenkova) · l.kuzenkova@list.ru
  • Federal State Budgetary Educational Institution of Higher Education "St. Petersburg State Pediatric Medical University", Ministry of Health of the Russian Federation, Saint Petersburg, Russia

    Contact: Study coordinator (Valentina Guzeva) · viktoryka@mail.ru
  • Federal State Budgetary Institution "V. A. Almazov National Medical Research Center" of the Ministry of Health of the Russian Federation, Saint Petersburg, Russia

    Contact: Study coordinator (Natalia Petrova) · natalja5@yandex.ru
  • State Autonomous Healthcare Institution of the Sverdlovsk Region "Regional Children's Clinical Hospital", Yekaterinburg, Russia

    Contact: Study coordinator (Olga Lvova) · olvova@bk.ru
מובילי המחקר
  • Arina V Zinkina-Orikhan, PhD

    Study Director

    Director of Clinical Development Department, BIOCAD