A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
מצבים רפואיים
Spinal Muscular Atrophy · SMA · Spinal Muscular Atrophy Type 2 · Spinal Muscular Atrophy Type 3 · Neuromuscular Manifestations · Anti-myostatin
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Phoenix Children's Hospital, Phoenix, Arizona, United States
Children's Hospital of Orange County (CHOC), Orange, California, United States
Stanford Neuroscience Health Center (SNHC), Palo Alto, California, United States
Children's Hospital Colorado, Aurora, Colorado, United States
Children's Healthcare of Atlanta, Atlanta, Georgia, United States
University of Iowa, Iowa City, Iowa, United States
Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids, Michigan, United States
Contact: Study coordinator (Rosa Sifontes-Escamilla) · rosa.sifontes-escamilla@helendevoschildrens.org · 616-486-6342Atrium Health Wake Forest Baptist, Winston-Salem, North Carolina, United States
The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Le Bonheur Children's Hospital, Memphis, Tennessee, United States
University of Texas Southwestern Medical Center, Dallas, Texas, United States
Neurology Rare Disease Center, Flower Mound, Texas, United States
Cook Children's Medical Center, Fort Worth, Texas, United States
Texas Children's Hospital (TCH)-Clinical Care Center (CCC), Houston, Texas, United States
UZ Gent, Ghent, East-Flanders, Belgium
UZ Leuven - Campus Gasthuisberg, Leuven, Belgium
CHR Citadelle, Liège, Belgium
Hopital Trousseau - I-Motion, Paris, France
Fondazione I.R.C.C.S. - Istituto Neurologico Carlo Besta, Milan, Italy
Centro Clinico NeMO Milano - Fondazione Serena Onlus, Milan, Italy
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy
Universitair Medisch Centrum Utrecht, Utrecht, Netherlands
Hospital Sant Joan de Déu Barcelona, Barcelona, Spain
Hospital Universitari i Politecnico La Fecnic La Fe, Valencia, Spain
Leeds General Infirmary Children's Research Department, Leeds, West Yorkshire, United Kingdom