Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Pompe Disease (Late-onset)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Chinese PLA General Hospital, Beijing, China
Contact: Study coordinator (Xinting Liu) · lxting0531@163.com · 16601558283
Contact: Principal Investigator (Guang Yang)

Study leads

Guang Yang
Study Chair
Chinese PLA General Hospital
Guang Yang
Principal Investigator
Chinese PLA General Hospital

View source on ClinicalTrials.gov

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