Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Abroad (travel likely)RecruitingPHASE2

Conditions

Pompe Disease

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • University of California - Irvine Medical Center, Irvine, California, United States

  • University of Florida (UF) - Gainesville, Gainesville, Florida, United States

  • Emory University Hospital, Atlanta, Georgia, United States

  • Washington University in St. Louis, St Louis, Missouri, United States

  • Duke University Medical Center, Durham, North Carolina, United States

  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

  • University of Pennsylvania, Philadelphia, Pennsylvania, United States

  • University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States

  • Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax, Virginia, United States

  • UZ Leuven, Leuven, Belgium

  • Aarhus University Hospital, Aarhus, Denmark

  • HLC Hopital Pierre Wertheimer, Bron, France

  • AP-HP Hopital Raymond Poincare, Garches, France

  • Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille, France

  • CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice, France

  • Universitaetsklinikum Halle (Saale), Halle, Germany

  • SphinCS GmbH, Höchheim, Germany

  • Klinikum der Ludwig-Maximilians-Universitaet Muenchen, München, Germany

  • A.O.U. Policlinico "G. Martino", Messina, Italy

  • AOU Citta della Salute e della Scienza di Torino - Ospedale le Molinette, Torino, Italy

  • Erasmus MC, GE Rotterdam, GE Rotterdam, Netherlands

  • Hospital Universitario 12 de Octubre, Madrid, Spain

  • Hospital Universitari i Politecnic La Fe, Valencia, Spain

  • Queen Elizabeth Hospital Birmingham, Birmingham, United Kingdom

  • National Hospital for Neurology & Neurosurgery, London, United Kingdom

  • Royal Free London NHS Foundation Trust, London, United Kingdom

  • Royal Victoria Infirmary, Newcastle upon Tyne, United Kingdom

  • Salford Royal Hospital, Salford, United Kingdom