Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Conditions
Pompe Disease
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
University of California - Irvine Medical Center, Irvine, California, United States
University of Florida (UF) - Gainesville, Gainesville, Florida, United States
Emory University Hospital, Atlanta, Georgia, United States
Washington University in St. Louis, St Louis, Missouri, United States
Duke University Medical Center, Durham, North Carolina, United States
Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
University of Pennsylvania, Philadelphia, Pennsylvania, United States
University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax, Virginia, United States
UZ Leuven, Leuven, Belgium
Aarhus University Hospital, Aarhus, Denmark
HLC Hopital Pierre Wertheimer, Bron, France
AP-HP Hopital Raymond Poincare, Garches, France
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille, France
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice, France
Universitaetsklinikum Halle (Saale), Halle, Germany
SphinCS GmbH, Höchheim, Germany
Klinikum der Ludwig-Maximilians-Universitaet Muenchen, München, Germany
A.O.U. Policlinico "G. Martino", Messina, Italy
AOU Citta della Salute e della Scienza di Torino - Ospedale le Molinette, Torino, Italy
Erasmus MC, GE Rotterdam, GE Rotterdam, Netherlands
Hospital Universitario 12 de Octubre, Madrid, Spain
Hospital Universitari i Politecnic La Fe, Valencia, Spain
Queen Elizabeth Hospital Birmingham, Birmingham, United Kingdom
National Hospital for Neurology & Neurosurgery, London, United Kingdom
Royal Free London NHS Foundation Trust, London, United Kingdom
Royal Victoria Infirmary, Newcastle upon Tyne, United Kingdom
Salford Royal Hospital, Salford, United Kingdom