Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Abroad (travel likely)RecruitingPHASE1, PHASE2
Conditions
Spinal Muscular Atrophy
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Peking University， First Hospital, Department of Pediatrics, Beijing, China
Contact: Principal Investigator (Hui Xiong)Bayi Children's Hospital, Seventh Medical Center, PLA general hospital, Beijing, China
Contact: Principal Investigator (Zhicun Feng)Shengjing Hospital of China Medical University, Shenyang, China
Contact: Principal Investigator (Hua Wang)Children's Hospital of Soochow University, Suzhou, China
Contact: Principal Investigator (Jihong Tang)