Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

Abroad (travel likely)Recruiting

Conditions

Spinal Muscular Atrophy

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

St. Jude Children's Research Hospital, Memphis, Tennessee, United States
Contact: Study coordinator (Jean Laboe, RN) · referralinfo@stjude.org · 901-595-1693
Contact: Principal Investigator (Richard Finkel, MD)

Study leads

Richard Finkel, MD
Principal Investigator
St. Jude Children's Research Hospital

View source on ClinicalTrials.gov

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