Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Spinal Muscular Atrophy Type I

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Hospital de Clínicas de Porto Alegre, Porto Alegre, Rio Grande do Sul, Brazil

Study leads
  • May Orfali, MD

    Study Director

    Gemma Biotherapeutics