Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Severe Sickle Cell Disease · Bone Marrow Failure Syndromes · Metabolic Disorders · Immunologic Disorders · Hemoglobinopathies · Non-malignant Disorders

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Yale School of Medicine, New Haven, Connecticut, United States

    Contact: Study coordinator (Lakshmanan Krishnamurti, MD)
    Contact: Principal Investigator (Lakshmanan Krishnamurti, MD)
  • Nemours Children's Health, Wilmington, Delaware, United States

    Contact: Study coordinator (Emi Caywood, MD) · 800-416-4441
    Contact: Principal Investigator (Emi Caywood, MD)
  • Helen DeVos Children's Hospital, Grand Rapids, Michigan, United States

    Contact: Study coordinator (Troy Quigg, DO)
    Contact: Principal Investigator (Troy Quigg, DO)
  • Washington University School of Medicine, St Louis, Missouri, United States

    Contact: Study coordinator (Shalini Shenoy, MD) · shalinishenoy@wustl.edu · 314-454-6018
    Contact: Study coordinator (Ian Snyder, BS, CCRP) · ian.s@wustl.edu · 314-273-5953
    Contact: Principal Investigator (Shalini Shenoy, MD)
Study leads
  • Shalini Shenoy, MD

    Principal Investigator

    Washington University School of Medicine