Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Conditions
Primary Immunodeficiency (PID) · Congenital Bone Marrow Failure Syndromes · Inherited Metabolic Disorders (IMD) · Hereditary Anemias · Inflammatory Conditions · Systemic Juvenile Idiopathic Arthritis (sJIA) · Juvenile Rheumatoid Arthritis (JRA)
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
Paulina Horvei, MD (Sub-investigator)Randy Windreich, MD (Sub-investigator)Archana Ramgopal, DO (Sub-investigator)
Study leads
Paul Szabolcs, MD
Principal Investigator
University of Pittsburgh