Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Abroad (travel likely)RecruitingPHASE2

Conditions

Primary Immunodeficiency (PID) · Congenital Bone Marrow Failure Syndromes · Inherited Metabolic Disorders (IMD) · Hereditary Anemias · Inflammatory Conditions · Systemic Juvenile Idiopathic Arthritis (sJIA) · Juvenile Rheumatoid Arthritis (JRA)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States

    Contact: Study coordinator (Shawna McIntyre, RN) · mcintyresm@upmc.edu · 412-692-5552
    Paulina Horvei, MD (Sub-investigator)
    Randy Windreich, MD (Sub-investigator)
    Archana Ramgopal, DO (Sub-investigator)
Study leads
  • Paul Szabolcs, MD

    Principal Investigator

    University of Pittsburgh