Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Abroad (travel likely)Recruiting

Conditions

Primary Immunodeficiency (PID) · Congenital Bone Marrow Failure Syndromes · Inherited Metabolic Disorders (IMD) · Hereditary Anemias · Inflammatory Conditions

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States

    Contact: Study coordinator (Shawna McIntyre, RN) · mcintyresm@upmc.edu · 412-692-5552
    Jessie Barnum, MD (Sub-investigator)
    Craig Byersdorfer, MD (Sub-investigator)
    Maria Escolar, MD (Sub-investigator)
    Elizabeth Stenger, MD (Sub-investigator)
    Randy Windreich, MD (Sub-investigator)
Study leads
  • Paul Szabolcs, MD

    Principal Investigator

    UPMC Children's Hospital of Pittsburgh