Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett Syndrome

Abroad (travel likely)RecruitingPHASE3

Conditions

Rett Syndrome

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Boston Children's Hospital, Boston, Massachusetts, United States
Study coordinator · RettResearch@childrens.harvard.edu

Study leads

Medical Monitor, M.D.
Study Director
Taysha Gene Therapies

View source on ClinicalTrials.gov

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