A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
Conditions
GM2 Gangliosidosis · Niemann-Pick Type C Disease
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Associação Hospitalar de Prot à Infância Dr. Raul Carneiro, Água Verde, Curitiba, Brazil
Contact: Study coordinator (Daniel Almeida do Valle) · daniel.valle@hpp.org.br · +55 (41) 2108-3861 - option 3Contact: Principal Investigator (Daniel Almeida do Valle)Hospital de Clinicas de Porto Alegre, Porto Alegre, Rio Grande do Sul, Brazil
Contact: Principal Investigator (Roberto Giugliani, Prof. Dr.)Instituto Nacional de Saúde da Mulher, da Criança e do Adolescente Fernandes Figueira, Rio de Janeiro, Brazil
Contact: Principal Investigator (Dafne Horovitz)