A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
מצבים רפואיים
Duchenne Muscular Dystrophy (DMD)
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
University Hospital Gent, Ghent, Belgium
Contact: Principal Investigator (Nicolas Deconinck)UZ Leuven, Leuven, Belgium
Contact: Principal Investigator (Liesbeth De Waele)Centre Hospitalier Régional de la Citadelle, Liège, Belgium
Contact: Principal Investigator (Aurore Daron)IRCCS Ospedale San Raffaele, Milan, Italy
Contact: Principal Investigator (Stefano Previtali)Ospedale Pediatrico Bambino Gesu, Rome, Italy
Contact: Principal Investigator (Adele D'Amico)Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Rome, Italy
Contact: Study coordinator (Eugenio Maria Mercuri) · eugeniomaria.mercuri@policlinicogemelli.it · 06 3015 4860Contact: Principal Investigator (Eugenio Maria Mercuri)Leids Universitair Medisch Centrum, Leiden, Netherlands
Contact: Principal Investigator (Erik Niks)Stichting Radboud Universitair Medisch Centrum, Nijmegen, Netherlands
Contact: Principal Investigator (Saskia Houwen)Hospital Universitario Vall d'Hebron, Barcelona, Spain
Contact: Principal Investigator (David Gomez Andres)Hospital Sant Joan de Deu, Barcelona, Spain
Contact: Principal Investigator (Andres Nascimento)Leeds General Infirmary, Leeds, United Kingdom
Contact: Principal Investigator (Cristina Martos Lozano)Alder Hey Children's NHS Foundation Trust, Liverpool, United Kingdom
Contact: Principal Investigator (Rajesh Madhu)Great Ormond Street Hospital for Children, London, United Kingdom
Contact: Principal Investigator (Giovanni Baranello)Royal Manchester Children's Hospital, Manchester, United Kingdom
Contact: Principal Investigator (Gary McCullagh)Oxford University Hospitals NHS Foundation Trust, Oxford, United Kingdom
Contact: Principal Investigator (Laurent Servais)
מובילי המחקר
Entrada Therapeutics Clinical Trials
Study Director
Entrada Therapeutics, Inc.