A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
מצבים רפואיים
Duchenne Muscular Dystrophy
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Aravindhan Veerapandiyan, MD)University of California, Los Angeles Medical Center, Los Angeles, California, United States
Contact: Principal Investigator (Perry Shieh, MD, PhD)University of California, Davis, Sacramento, California, United States
Contact: Principal Investigator (Craig McDonald, MD)University of California, San Diego, California, United States
Contact: Principal Investigator (Chamindra Laverty, MD)Rare Disease Research, Atlanta, Georgia, United States
Contact: Principal Investigator (Renata Shih, MD)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Study coordinator (Nancy Kuntz, MD)Washington University in St. Louis, St Louis, Missouri, United States
Contact: Study coordinator (Natalie Goedeker) · neuromusclepediatricresearch@wustl.edu · 314-362-4919Contact: Principal Investigator (Craig Zaidman, MD)Nationwide Children's Hospital, Columbus, Ohio, United States
Contact: Principal Investigator (Kevin Flanigan, MD)Oregon Health and Sciences University, Portland, Oregon, United States
Contact: Principal Investigator (Erika Finanger, MD)Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (John Brandsema, MD)Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud, MD)Seattle Children's Hospital, Seattle, Washington, United States
Contact: Principal Investigator (Alicia Henriquez, MD)The Hospital for Sick Children, Toronto, Ontario, Canada
Contact: Principal Investigator (Hernan Gonorazky, MD)Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy
Contact: Study coordinator (Lorenzo Stivala) · lorenzo.stivala@policlinicogemelli.it · +39 063-015-6330Contact: Principal Investigator (Eugenio Mercuri, MD, PhD)Great Ormond Street Hospital, London, United Kingdom
Contact: Principal Investigator (Francesco Muntoni, MD)
מובילי המחקר
Solid Bio Clinical Trials
Study Director
Solid Biosciences