A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
Conditions
Facioscapulohumeral Muscular Dystrophy
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
David Geffen School of Medicine at University of California, Los Angeles, Los Angeles, California, United States
Contact: Principal Investigator (Perry Shieh, MD, PhD)Rare Disease Research, Atlanta, Georgia, United States
Contact: Principal Investigator (Renata Shih, MD)Kennedy Krieger Institute, Center for Genetic Muscle Disorders, Baltimore, Maryland, United States
Contact: Principal Investigator (Doris G Leung, MD, PhD)University of Massachusetts Chan Medical School, Worcester, Massachusetts, United States
Contact: Study coordinator (Catherine Douthwright) · Catherine.Douthwright@umassmed.edu · 508-865-1524Utah Program for Inherited Neuromuscular Disorders - University of Utah, Salt Lake City, Utah, United States
Contact: Principal Investigator (Russell Butterfield, MD, PhD)Royal Alfred Hospital, Sydney, New South Wales, Australia
Contact: Principal Investigator (Katrina Anne Morris, BMedSCI, MBBS(Hons), PhD,FRACP)Pacific Clinical Research Network, Auckland, New Zealand