A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
מצבים רפואיים
Muscular Atrophy, Spinal
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Children's Hospital of Orange County, Orange, California, United States
Contact: Principal Investigator (Julian Thomas)Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto, California, United States
Contact: Principal Investigator (John Day)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Nancy Kuntz)Boston Children's Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Basil T Darras)Helen DeVos Children's Hospita, Grand Rapids, Michigan, United States
Contact: Principal Investigator (Jena Krueger)Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey, Pennsylvania, United States
Contact: Principal Investigator (Dustin Paul)Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (Patrick Cahill)Texas Childrens Hospital Houston, Houston, Texas, United States
Contact: Principal Investigator (David Bauer)Stacey Hall Developmental Pediatrics, Charlottesville, Virginia, United States
Contact: Principal Investigator (Rebecca J Scharf)Children's Hospital of the King's Daughters_Norfolk, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud)Hôpital Raymond Poincaré, Garches, Hauts De Seine, France
Contact: Principal Investigator (Marta Gomez)Universitaetsklinikum Essen, Essen, Germany
Contact: Principal Investigator (Tim Hagenacker)Fondazione Serena Onlus - Centro Clinico Nemo_Milano, Milan, Italy
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy
Szpital Specjalistyczny im. L.Rydygiera w Krakowie, Krakow, Poland
Contact: Principal Investigator (Ryszard Nowak)Instytut Centrum Zdrowia Matki Polki, Lodz, Poland
Contact: Principal Investigator (Przyslo Lukasz)Hospital Universitario La Paz, Madrid, Spain
Contact: Principal Investigator (Maria Garcia Romero)Hospital Universitari i Politecnic La Fe_Valencia, Valencia, Spain
Contact: Principal Investigator (Juan Francisco Vazquez Costa)Royal Hallamshire Hospital Neurology Department, Sheffield, South Yorkshire, United Kingdom
Contact: Principal Investigator (Chanma Hewadduma)
מובילי המחקר
Medical Director
Study Director
Biogen