A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

University of Arkansas for Medical Sciences, Little Rock, Arkansas, United States

Children's Hospital of Colorado, Aurora, Colorado, United States

University of Florida Pediatrics, Gainesville, Florida, United States

Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta, Georgia, United States

Ann and Robert H. Lurie Children Hospital of Chicago, Chicago, Illinois, United States

Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids, Michigan, United States

Columbia University Medical Center, New York, New York, United States

Children'S Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

The University of Texas Southwestern Medical Center at Dallas, Dallas, Texas, United States

Cook Children's Jane and John Justin Neurosciences Center, Fort Worth, Texas, United States

Children's Hospital of the King's Daughter, Norfolk, Virginia, United States

Charité - Universitätsmedizin Berlin SPZ Abteilung Neuropaediatrie, Berlin, Germany

UKGM Standort Gießen, Giessen, Germany

Uniwersyteckie Centrum Kliniczne, Uniwersyteckie Centrum Kliniczne, Poland

Instytut Pomnik Centrum Zdrowia Dziecka, Warsaw, Poland

Great Ormond Street Hospital For Children, London, United Kingdom