A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Conditions
Muscular Atrophy, Spinal
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Locations
Children's Hospital of Orange County, Orange, California, United States
Contact: Principal Investigator (Julian Thomas)Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto, California, United States
Contact: Principal Investigator (John Day)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Nancy Kuntz)Boston Children's Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Basil T Darras)Helen DeVos Children's Hospita, Grand Rapids, Michigan, United States
Contact: Principal Investigator (Jena Krueger)Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey, Pennsylvania, United States
Contact: Principal Investigator (Dustin Paul)Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (Patrick Cahill)Texas Childrens Hospital Houston, Houston, Texas, United States
Contact: Principal Investigator (David Bauer)Stacey Hall Developmental Pediatrics, Charlottesville, Virginia, United States
Contact: Principal Investigator (Rebecca J Scharf)Children's Hospital of the King's Daughters_Norfolk, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud)Hôpital Raymond Poincaré, Garches, Hauts De Seine, France
Contact: Principal Investigator (Marta Gomez)Universitaetsklinikum Essen, Essen, Germany
Contact: Principal Investigator (Tim Hagenacker)Fondazione Serena Onlus - Centro Clinico Nemo_Milano, Milan, Italy
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy
Szpital Specjalistyczny im. L.Rydygiera w Krakowie, Krakow, Poland
Contact: Principal Investigator (Ryszard Nowak)Instytut Centrum Zdrowia Matki Polki, Lodz, Poland
Contact: Principal Investigator (Przyslo Lukasz)Hospital Universitario La Paz, Madrid, Spain
Contact: Principal Investigator (Maria Garcia Romero)Hospital Universitari i Politecnic La Fe_Valencia, Valencia, Spain
Contact: Principal Investigator (Juan Francisco Vazquez Costa)Royal Hallamshire Hospital Neurology Department, Sheffield, South Yorkshire, United Kingdom
Contact: Principal Investigator (Chanma Hewadduma)
Study leads
Medical Director
Study Director
Biogen