A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Abroad (travel likely)RecruitingPHASE1

Conditions

Muscular Atrophy, Spinal

Simple summaryAI-assisted

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Locations
  • Children's Hospital of Orange County, Orange, California, United States

    Study coordinator · 714-509-3605
    Contact: Principal Investigator (Julian Thomas)
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto, California, United States

    Study coordinator · 650-723-5152
    Contact: Principal Investigator (John Day)
  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

    Study coordinator · 312-227-3550
    Contact: Principal Investigator (Nancy Kuntz)
  • Boston Children's Hospital, Boston, Massachusetts, United States

    Study coordinator · 617-355-8036
    Contact: Principal Investigator (Basil T Darras)
  • Helen DeVos Children's Hospita, Grand Rapids, Michigan, United States

    Study coordinator · 616-391-2241
    Contact: Principal Investigator (Jena Krueger)
  • Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey, Pennsylvania, United States

    Study coordinator · 717-232-5443
    Contact: Principal Investigator (Dustin Paul)
  • Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

    Study coordinator · 215-590-3174
    Contact: Principal Investigator (Patrick Cahill)
  • Texas Childrens Hospital Houston, Houston, Texas, United States

    Study coordinator · 832-822-1750
    Contact: Principal Investigator (David Bauer)
  • Stacey Hall Developmental Pediatrics, Charlottesville, Virginia, United States

    Study coordinator · 434-924-8184
    Contact: Principal Investigator (Rebecca J Scharf)
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk, Virginia, United States

    Study coordinator · 757-668-7000
    Contact: Principal Investigator (Crystal Proud)
  • Hôpital Raymond Poincaré, Garches, Hauts De Seine, France

    Study coordinator · +33147104684
    Contact: Principal Investigator (Marta Gomez)
  • Universitaetsklinikum Essen, Essen, Germany

    Study coordinator · 49 201 7230
    Contact: Principal Investigator (Tim Hagenacker)
  • Fondazione Serena Onlus - Centro Clinico Nemo_Milano, Milan, Italy

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy

  • Szpital Specjalistyczny im. L.Rydygiera w Krakowie, Krakow, Poland

    Study coordinator · 48604565621
    Contact: Principal Investigator (Ryszard Nowak)
  • Instytut Centrum Zdrowia Matki Polki, Lodz, Poland

    Study coordinator · +48606989185
    Contact: Principal Investigator (Przyslo Lukasz)
  • Hospital Universitario La Paz, Madrid, Spain

    Study coordinator · +34917277388
    Contact: Principal Investigator (Maria Garcia Romero)
  • Hospital Universitari i Politecnic La Fe_Valencia, Valencia, Spain

    Study coordinator · 34 961 24 55 42
    Contact: Principal Investigator (Juan Francisco Vazquez Costa)
  • Royal Hallamshire Hospital Neurology Department, Sheffield, South Yorkshire, United Kingdom

    Study coordinator · +441142713708
    Contact: Principal Investigator (Chanma Hewadduma)
Study leads
  • Medical Director

    Study Director

    Biogen