A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

Abroad (travel likely)RecruitingPHASE3

Conditions

Muscular Atrophy, Spinal

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago, Illinois, United States

    Study coordinator · 312-227-4637
    Contact: Principal Investigator (Nancy Kuntz)
  • Neurology Rare Disease Center, Flower Mound, Texas, United States

    Study coordinator · 214-456-4267
    Contact: Principal Investigator (Diana Castro)
  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk, Virginia, United States

    Study coordinator · proud.research@chkd.org · 757-668-6981
    Contact: Principal Investigator (Crystal Proud)
  • Childrens Hospital of Fudan University_Shanghai, Shanghai, China

  • Japan Institute for Health Security National Center for Global Health and Medicine, Tokyo, Japan

Study leads
  • Medical Director

    Study Director

    Biogen