KHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases
מצבים רפואיים
Mitochondrial Diseases · Maternally Inherited Diabetes and Deafness (MIDD) · Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke-like Episodes (MELAS) · Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Massachusetts General Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Amel Karaa, Dr.)Cleveland Clinic Neurological Institute Mellen Center, Cleveland, Ohio, United States
Contact: Principal Investigator (Sumit Parikh, Dr.)The University of Texas Health Science Center at Houston, Houston, Texas, United States
Contact: Study coordinator (Antoinette Bernal Tent) · antoinette.w.bernaltent@uth.tmc.edu · (713) 500-6991Contact: Principal Investigator (Mary Koenig, Dr.)Sam Nicholas Russo, Dr. (Sub-investigator)Rigshospitalet, University of Copenhagen, Kopenhagen, Region Sjælland, Denmark
Contact: Study coordinator (Emma Roerbaek Larsen) · emma.roerbaek.larsen.01@regionh.dk · +4535453545Contact: Principal Investigator (Nicolai Rasmus Preisler, Dr.)CHU de Bordeaux - Hôpital Pellegrin Service Gynecologie Obstetrique, Bordeaux, Gironde, France
Contact: Study coordinator (Samira Madi Radjabou) · samira.madi-radjabou@chu-bordeaux.fr · +33540451129 x51129Contact: Principal Investigator (Aurelien Trimouille, Dr.)Groupe Hospitalier Pitie-Salpetriere - Charles-Foix Clinical Investigation Center Paris-Est, Paris, Paris, France
Contact: Study coordinator (Sarah Taieb Tamacha) · sarah.taieb-tamacha@icm-institute.org · +33473750750Contact: Principal Investigator (Fanny Mochel, Dr.)Klinikum der Universität München Friedrich-Baur-Institut, München, Germany
Contact: Study coordinator (Natalie Adriana Villalobos Trigueros) · natalie.villalobos@med.uni-muenchen.de · +49 89/4400-57402Contact: Principal Investigator (Thomas Klopstock, Prof. Dr.)Boriana Buechner, Dr. (Sub-investigator)Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy
Contact: Principal Investigator (Costanza Lamperti, Dr.)Radboud University Medical Center, Nijmegen, Gelderland, Netherlands
Contact: Study coordinator (Evertine Abbink, MD, PhD) · evertine.abbink@radboudumc.nl · +31 24 3618819Contact: Principal Investigator (Mirian Janssen, MD, PhD)University College London Hospitals NHS Foundation Trust National Hospital for Neurology and Neurosurgery, London, Greater London, United Kingdom
Contact: Principal Investigator (Robbert Pitceathly, Dr.)