A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's Ataxia
מצבים רפואיים
Friedreich Ataxia
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
UCLA Neurology Outpatient Clinic at Westwood, Los Angeles, California, United States
Contact: Principal Investigator (Susan Perlman)Norman Fixel Institute for Neurological Diseases UF Health, Gainesville, Florida, United States
Contact: Principal Investigator (Sankarsubramoney Subramony)USF Health Morsani College of Medicine Department of Neurology, Tampa, Florida, United States
Contact: Principal Investigator (Theresa Zesiewicz)Children's Hospital of Philadelphia - Buerger Center for Advanced Pediatric Care - PIN, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (David Robinson Lynch)St. Jude Children's Research Hospital - PIN, Memphis, Tennessee, United States
Contact: Principal Investigator (Richard Finkel)CHKD's Health Center - South Campus - PIN, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud)Seattle Children's Hospital, Seattle, Washington, United States
Contact: Principal Investigator (Alicia Henriquez)Sydney Children's Hospital, Randwick, New South Wales, Australia
Murdoch Childrens Research Institute (MCRI), Parkville, Victoria, Australia
Universitätsklinikum Innsbruck, Innsbruck, Austria
Contact: Principal Investigator (Sylvia M Boesch)L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME, Brasília, Federal District, Brazil
Contact: Principal Investigator (Ingrid Faber Faber de Vasconcellos)University of Campinas (UNICAMP) School of Medical Sciences, Campinas, São Paulo, Brazil
Contact: Principal Investigator (Marcondes Franca)PSEG Centro de Pesquisa Clinica, São Paulo, São Paulo, Brazil
Contact: Principal Investigator (Paulo Victor Sgobbi de Souza)McGill University, Montreal, Quebec, Canada
Contact: Principal Investigator (Maryam Oskoui)CHU de Quebec -Universite Laval, Québec, Quebec, Canada
Contact: Principal Investigator (Nicolas Chrestian)Rigshospitalet - Juliane Marie Centret (JMC) Copenhagen, Copenhagen, Denmark
Contact: Principal Investigator (Alfred Peter Born)CHU de Montpellier- Hôpital Gui De Chauliac, Montpellier, Hérault, France
Contact: Principal Investigator (Agathe Roubertie)AP-HP - Hôpital Armand Trousseau, Paris, France
Contact: Principal Investigator (Florence Renaldo)Universitätsklinikum Aachen, Aachen, North Rhine-Westphalia, Germany
Contact: Principal Investigator (Kathrin Reetz)UKGM - Universitätsklinikum Giessen und Marburg GmbH - Standort Gießen, Giessen, Germany
Contact: Principal Investigator (Andreas Hahn)Universitätsklinikum Hamburg Eppendorf, Hamburg, Germany
Contact: Principal Investigator (Deike Weiss)All India Institute of Medical Sciences (AIIMS) - New Delhi, New Delhi, National Capital Territory of Delhi, India
CHI at Temple Street, Dublin, Ireland
Contact: Principal Investigator (Declan O'Rourke)Ospedale Pediatrico Bambino Gesù IRCCS, Rome, Lazio, Italy
Contact: Principal Investigator (Gessica Vasco)IRCCS Eugenio Medea - Polo. Scientifico Veneto, Conegliano, Veneto, Italy
Contact: Principal Investigator (Gabriella Paparella)Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy
Contact: Principal Investigator (Isabella Moroni)Radboud Universitair Medisch Centrum, Nijmegen, Netherlands
Contact: Principal Investigator (Nienke van Os)King Faisal Specialist Hospital & Research Centre, Riyadh, Ar Riya, Saudi Arabia
Hospital Sant Joan de Deu - PIN, Espluges de Llobregat, Barcelona, Spain
Contact: Principal Investigator (Alejandra Darling)Hospital Universitario La Paz - PPDS, Madrid, Spain
Contact: Principal Investigator (Maria del Mar Garcia Romero)Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi, Istanbul, Turkey (Türkiye)
University College Hospital - PPDS, London, Lincolnshire, United Kingdom
Contact: Principal Investigator (Shpresa Pula)John Radcliffe Hospital, Oxford, Oxfordshire, United Kingdom
Contact: Principal Investigator (Andrea Németh)Sheffield Children's Hospital - PPDS, Sheffield, South Yorkshire, United Kingdom
Contact: Principal Investigator (Santosh Ravindra Mordekar)
מובילי המחקר
Medical Director
Study Director
Biogen