A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
Conditions
Myotonic Dystrophy Type 1 (DM1)
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Stanford Neuromuscular Research, San Carlos, California, United States
University of Florida Clinical Research Center, Gainesville, Florida, United States
University of Kansas Medical Center, Fairway, Kansas, United States
Boston Children's Hospital, Boston, Massachusetts, United States
Washington University School of Medicine / St. Louis Children's Hospital, St Louis, Missouri, United States
Wake Forest Baptist Health, Winston-Salem, North Carolina, United States
University of Pennsylvania, Philadelphia, Pennsylvania, United States
Virginia Commonwealth University (Sanger Hall), Richmond, Virginia, United States
Wesley Research Institute, Auchenflower, Australia
Neuroscience Clinical Trials Unit, Alfred Brain, Melbourne, Australia
Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg, Leuven, Belgium
Hopital de Chicoutimi, Chicoutimi, Canada
Altasciences Montreal, Montreal, Canada
McGIll University, Montreal, Canada
University of Ottawa, Ottawa, Canada
CHU Research Centre of Quebec, Québec, Canada
Neuromuscular Reference Center Institute of Myology, Paris, France
Ludwig Maximilians Universitaet Muenchen, München, Germany
Centro Clinico NeMO, Milan, Italy
Maastricht University Medical Center, Maastricht, Netherlands
Hospital Universitario y Politécnico La Fe, Valencia, Spain
Clinical Research Facility, Queen Elizabeth University Hospital, Glasgow, United Kingdom
Leonard Wolfson Experimental Neurology Centre CRF, London, United Kingdom
St. George's University Hospital, London, United Kingdom
Salford Royal Hospital, Salford, United Kingdom
Royal Hallamshire Hospital, Sheffield, United Kingdom