Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1
Conditions
Myotonic Dystrophy Type 1 (DM1)
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Locations
Stanford University, Stanford, California, United States
Contact: Principal Investigator (Dr. John Day, MD, PhD)University of Florida College of Medicine, Gainesville, Florida, United States
Contact: Principal Investigator (Dr. Sub Subramony, MD)Indiana University School of Medicine, Indianapolis, Indiana, United States
Contact: Principal Investigator (Laurie Gutmann, MD)University of Iowa, Iowa City, Iowa, United States
Contact: Principal Investigator (Andrea Swenson, MD)Washington University in St. Louis, St Louis, Missouri, United States
Contact: Principal Investigator (Dr. Craig Zaidman, MD)University of Rochester Medical Center, Rochester, New York, United States
Contact: Principal Investigator (Dr. Joahnna Hamel, MD)Neurology Rare Disease Center, Denton, Texas, United States
Contact: Principal Investigator (Diana Castro, MD)Virginia Commonwealth University (VCU), Richmond, Virginia, United States
Contact: Principal Investigator (Nicholas Johnson, M.D., M.Sci., FAAN)St. Vincent's Hospital, Fitzroy, Victoria, Australia
Contact: Principal Investigator (Dr. Gayatri Jain)CHU de Nantes, Nantes, France
Contact: Principal Investigator (Yann Péréon, MD, PhD)Institut de Myologie, Paris, France
Contact: Principal Investigator (Dr. Guillaume Bassez)Charité - Universitätsmedizin Berlin, Berlin, Germany
Contact: Principal Investigator (Elisabetta Gazzerro, MD, PhD)Ludwig Maximilians University, Munich - Friedrich Baur Institut, Munich, Germany
Contact: Principal Investigator (Benedikt Schoser, MD)Stephan Wenninger, MD (Sub-investigator)Centro Clinico Nemo, Milan, Italy
Contact: Principal Investigator (Valeria Sansone, MD, PhD)Fondazione Policlinico Universitario A Gemelli-Rome, Rome, Italy
Contact: Principal Investigator (Marika Pane)Radboud Medical Center, Nijmegen, Netherlands
Contact: Principal Investigator (Karien Mul)NZCR Auckland, Auckland, New Zealand
Contact: Principal Investigator (Dr. Richard Roxburgh)University College London Hospitals, London, United Kingdom
Contact: Principal Investigator (Dr. Chris Turner)John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne, United Kingdom
Contact: Principal Investigator (Jordi Diaz-Manera)Salford Royal Hospital, Salford, United Kingdom
Contact: Principal Investigator (James Lilleker)