Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Myotonic Dystrophy Type 1 (DM1)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Stanford University, Stanford, California, United States

    Contact: Study coordinator (Lidia Choniawko) · lidiacho@stanford.edu
    Contact: Principal Investigator (Dr. John Day, MD, PhD)
  • University of Florida College of Medicine, Gainesville, Florida, United States

    Contact: Study coordinator (Debbye Landers) · debralanders@peds.ufl.edu
    Contact: Principal Investigator (Dr. Sub Subramony, MD)
  • Indiana University School of Medicine, Indianapolis, Indiana, United States

    Contact: Study coordinator (Patti Hogan, BSN RN, CCRA) · hoganpr@iu.edu
    Contact: Principal Investigator (Laurie Gutmann, MD)
  • University of Iowa, Iowa City, Iowa, United States

    Contact: Study coordinator (Heena Olade, RN, MSN) · heena-olalde@uiowa.edu
    Contact: Principal Investigator (Andrea Swenson, MD)
  • Washington University in St. Louis, St Louis, Missouri, United States

    Contact: Study coordinator (Natalie Goedeker) · ngoedeker@wustl.edu
    Contact: Principal Investigator (Dr. Craig Zaidman, MD)
  • University of Rochester Medical Center, Rochester, New York, United States

    Contact: Study coordinator (Jim Hilbert) · james_hilbert@urmc.rochester.edu
    Contact: Principal Investigator (Dr. Joahnna Hamel, MD)
  • Neurology Rare Disease Center, Denton, Texas, United States

    Contact: Study coordinator (Isabella Herman) · Research@neuromdcenter.com
    Contact: Principal Investigator (Diana Castro, MD)
  • Virginia Commonwealth University (VCU), Richmond, Virginia, United States

    Contact: Study coordinator (Jodie Howell) · Jodie.howell@vcuhealth.org
    Contact: Study coordinator (Anarosa Rezeq) · anarosa.rezeq@vcuhealth.org
    Contact: Principal Investigator (Nicholas Johnson, M.D., M.Sci., FAAN)
  • St. Vincent's Hospital, Fitzroy, Victoria, Australia

    Contact: Study coordinator (Alan Lai) · alan.lai@svha.org.au
    Contact: Principal Investigator (Dr. Gayatri Jain)
  • CHU de Nantes, Nantes, France

    Contact: Study coordinator (Marie-Agnès Sourdril) · marieagnes.sourdril@chu-nantes.fr
    Contact: Principal Investigator (Yann Péréon, MD, PhD)
  • Institut de Myologie, Paris, France

    Contact: Study coordinator (Asma Balloumi) · a.balloumi@institut-myologie.org
    Contact: Principal Investigator (Dr. Guillaume Bassez)
  • Charité - Universitätsmedizin Berlin, Berlin, Germany

    Contact: Study coordinator (Susanne Behr-Perst) · susanne.behr-perst@charite.de
    Contact: Principal Investigator (Elisabetta Gazzerro, MD, PhD)
  • Ludwig Maximilians University, Munich - Friedrich Baur Institut, Munich, Germany

    Contact: Study coordinator (Corinna Wirner-Piotrowski) · Corinna.Wirner@med.uni-muenchen.de
    Contact: Principal Investigator (Benedikt Schoser, MD)
    Stephan Wenninger, MD (Sub-investigator)
  • Centro Clinico Nemo, Milan, Italy

    Contact: Study coordinator (Maribel Evoli) · maribel.evoli@centrocliniconemo.it
    Contact: Principal Investigator (Valeria Sansone, MD, PhD)
  • Fondazione Policlinico Universitario A Gemelli-Rome, Rome, Italy

    Contact: Study coordinator (Maria Pirozzoli) · mariaceleste.pirozzoli@policlinicogemelli.it
    Contact: Principal Investigator (Marika Pane)
  • Radboud Medical Center, Nijmegen, Netherlands

    Contact: Study coordinator (Eline Sanders) · clinicalresearchunit@radboudumc.nl
    Contact: Principal Investigator (Karien Mul)
  • NZCR Auckland, Auckland, New Zealand

    Contact: Study coordinator (Miriam Rodrigues) · MRodrigues@adhb.govt.nz
    Contact: Principal Investigator (Dr. Richard Roxburgh)
  • University College London Hospitals, London, United Kingdom

    Contact: Study coordinator (Nikoletta Nikolenko) · n.nikolenko@nhs.net
    Contact: Principal Investigator (Dr. Chris Turner)
  • John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne, United Kingdom

    Contact: Study coordinator (Nicola McLarty) · nicola.mclarty1@nhs.net
    Contact: Principal Investigator (Jordi Diaz-Manera)
  • Salford Royal Hospital, Salford, United Kingdom

    Contact: Study coordinator (Bethan Blackledge) · Bethan.blackledge@nca.nhs.uk
    Contact: Principal Investigator (James Lilleker)