AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
מצבים רפואיים
Duchenne Muscular Dystrophy
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Principal Investigator (Aravindhan Veerapandiyan, MD)Stanford School of Medicine /Division of Neuromuscular Medicine, Palo Alto, California, United States
Contact: Principal Investigator (Carolina Tesi-Rocha, MD)Children's Hospital Colorado, Aurora, Colorado, United States
Contact: Principal Investigator (Michele Yang, MD)University of Florida, Gainesville, Florida, United States
Contact: Principal Investigator (Barry Byrne, MD)Rare Disease Research, Atlanta, Georgia, United States
Contact: Study coordinator (Maureen Ikpeoha) · maureen.ikpeoha@rarediseaseresearch.com · 470-666-1884Contact: Principal Investigator (Han Phan, MD)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Nancy L Kuntz, MD)University of Iowa, Iowa City, Iowa, United States
Contact: Principal Investigator (Dimah Saade, MD)University of Massachusetts Chan Medical School, Worcester, Massachusetts, United States
Contact: Principal Investigator (Eleonora D'Ambrosio, MD)Cincinnati Children's, Cincinnati, Ohio, United States
Contact: Principal Investigator (Cuixia Tian, MD)Oregon Health & Science University, Portland, Oregon, United States
Contact: Principal Investigator (Erika Finanger, MD)The University of Texas Southwestern Medical Center, Dallas, Texas, United States
Contact: Principal Investigator (Susan Iannaccone, MD)Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Contact: Principal Investigator (Crystal Proud, MD)Children's Hospital of Richmond at Virginia Commonwealth University, Richmond, Virginia, United States
Contact: Principal Investigator (Amy Harper, MD)Alberta Children's Hospital, Calgary, Alberta, Canada
Contact: Principal Investigator (Jean Mah, MD)BC Children's Hospital, Vancouver, British Columbia, Canada
Contact: Principal Investigator (Kathryn Selby, MD)Children's Hospital London Health Science Centre, London, Ontario, Canada
Contact: Principal Investigator (Craig Campbell, MD)Children's Hospital of Eastern Ontario, Ottawa, Ontario, Canada
Contact: Principal Investigator (Hugh McMillan, MD)