Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia

Abroad (travel likely)RecruitingPHASE1

Conditions

Friedreich Ataxia · Cardiomyopathies · Cardiac Hypertrophy · Myocardial Fibrosis

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Weill Cornell Medicine, New York, New York, United States
Contact: Study coordinator (Maddie Galbraith, BS) · meg4013@med.cornell.edu · 646-962-2672
Contact: Study coordinator (Niamh Savage, BS) · nis2049@med.cornell.edu · 646-962-5527
Contact: Principal Investigator (Ronald G Crystal, MD)

Study leads

Ronald G Crystal, MD
Principal Investigator
Weill Medical College of Cornell University

View source on ClinicalTrials.gov

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