An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia
Conditions
Friedreich Ataxia
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
University of California Los Angeles, Los Angeles, California, United States
Fixel Institute for Neurological Disease, University of Florida Health, Gainesville, Florida, United States
Morsani Center for Advanced Health Care, University of South Florida Health, Tampa, Florida, United States
University of Iowa, Iowa City, Iowa, United States
Uncommon Cures, Chevy Chase, Maryland, United States
Clinilabs Drug Development, Corp., Eatontown, New Jersey, United States
Ohio State University United States, Columbus, Ohio, United States
Children's Hospital of the University of Pennsylvania (CHOP), Philadelphia, Pennsylvania, United States
Study leads
Larimar Therapeutics, Inc.
Study Chair
Larimar Therapeutics, Inc.