Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures

Abroad (travel likely)RecruitingPHASE2

Conditions

Primary Immune Deficiency Disorder · Immune Deficiency Disease · Bone Marrow Failure · Short Telomere Length · Fanconi Anemia · Non Fanconi DNA-DSB Repair Disorder · Hoyeraal-Hreidarsson Syndrome · Dyskeratosis Congenita · Telomere Biology Disorder · Short Telomere Syndrome

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Johns Hopkins University, Baltimore, Maryland, United States

    Contact: Study coordinator (Megan Petrycki, MSN, RN) · mpetryc1@jhmi.edu
    Contact: Principal Investigator (Heather J Symons, MD)
Study leads
  • Heather J Symons, MD, MHS

    Principal Investigator

    Johns Hopkins University