Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

ישראלמגייס משתתפיםPHASE2, PHASE3

מצבים רפואיים

Duchenne Muscular Dystrophy

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation, Sacramento, California, United States

  • Rady Children's Hospital center - UCSD Department of Neuroscience, San Diego, California, United States

  • Connecticut Children's Medical Center, Neurology Division, Hartford, Connecticut, United States

  • Child Health Research Institute, Gainesville, Florida, United States

  • MD Rare Disease Research, LLC, Atlanta, Georgia, United States

  • University of Iowa Children's Hospital, Iowa City, Iowa, United States

  • Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111, St Louis, Missouri, United States

  • Shriners Hospitals for Children, Portland, Oregon, United States

  • The Children's Hospital of Philadelphia Colket Translational Research Building, Philadelphia, Pennsylvania, United States

  • Virginia Commonwealth University Childrens Hospital of Richmond at, Richmond, Virginia, United States

  • University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology, Leuven, Belgium

  • Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN), Liège, Belgium

  • Kinsmen Research Centre - Alberta Children's Hospital, Calgary, Alberta, Canada

  • The University of British Columbia, Children's and Womens Health Centre of BC Branch, Vancouver, British Columbia, Canada

  • Holland Bloorview Kids Rehabilitation Hospital, Toronto, Ontario, Canada

  • CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest, Nantes, France

  • Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette, Paris, France

  • Universitätsklinikum Essen - Kinder-und Jugendmedizin Neuropadiatrie, Essen, Germany

  • Klinik- und Poliklinik fur Kinder- und Jugendmedizin, Universitatsklinikum HamburgEppendorf, Martinistr. 52, Hamburg, Germany

  • Klinikum der Universitat Munchen, Campus Innenstadt, Lindwurmstr. 4, München, Germany

  • Institute of Neurology - Schneider Children's Medical Center of Israel Kaplan, 14, Petah Tikva, Israel

  • U.O.S.D. Centro Traslazionale di Miologia e Patologie Neurodegenerative, Building 16 - ground floor IRCCS Istituto Giannina Gaslini,, Genova, Italy

    Contact: Study coordinator (Claudio Bruno, MD) · claudio2246@gmail.com · +39 010 56362 2620
    Contact: Principal Investigator (Claudio Bruno, MD)
  • A.O.U. Policlinico G. Martino, U.O.C. Neurologia e Malattie Neuromuscolari, Messina, Italy

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, UOS di Neurologia Pediatrica, Milan, Italy

  • IRCCS Istituto Neurologico Carlo Besta, Milan, Italy

  • Centro Clinico NeMO Fondazione Serena ONLUS Area SUD, Milan, Italy

  • Ospedale Pediatrico Bambino Gesù, Malattie Neuromuscolari e Neurodegenerative, Roma, Italy

    Contact: Study coordinator (Enrico Bertini, MD) · enricosilvio.bertini@opbg.net
    Contact: Principal Investigator (Enrico Bertini, MD)
  • Fondazione Policlinico Universitario "A.Gemelli", UOC Neuropsichiatria Infantile, Roma, Italy

  • Leiden University Medical Center LUMC, Albinusdreef 2, Leiden, Netherlands

  • Radboud University Medical Centre, Nijmegen, Netherlands

  • Clinic of Neurology and Psychiatry for Children and Youth - Neurology Department Dr. Subotic 6a,, Belgrade, Serbia

  • Neuromuscular Pathology Unit - Hospital Sant Joan de Déu, Esplugues de Llobregat, Barcellona, Spain

  • Hospital Materno-Infantil, Barcelona, Spain

    Contact: Study coordinator (Francina Munell, MD) · francina.munell@vhir.org
    Contact: Principal Investigator (Francina Munell, MD)
  • Hospital Universitario Virgen del Rocio, Seville, Spain

  • Hospital Universitari i Politècnic La Fe - Servicio Neurologia, Valencia, Spain

  • Alder Hey Children's Hospital NHS Trust, Liverpool, UK, United Kingdom

  • The Robert Jones and Agnes Hunt Orthopaedic Hospital NHS Foundation Trust, Gobowen, United Kingdom

  • UCL Great Ormond Street Institute of Child Health, Dubowitz Neuromuscular Centre and MRC Centre for NMD, London, United Kingdom

  • The John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne, United Kingdom