A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia

חו"ל (דורש נסיעה)הושלםPHASE3

מצבים רפואיים

Achondroplasia

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • Children's Hospital & Research Center Oakland, Oakland, California, United States

  • Harbor - UCLA Medical Center, Torrance, California, United States

  • Alfred I. duPont Hospital for Children, Wilmington, Delaware, United States

  • Emory University, Decatur, Georgia, United States

  • Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

  • Johns Hopkins University, Baltimore, Maryland, United States

  • University of Missouri, Columbia, Missouri, United States

  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

  • Baylor College of Medicine, Houston, Texas, United States

  • Seattle Children's Hospital, Seattle, Washington, United States

  • Medical College of Wisconsin, Children's Hospital, Milwaukee, Wisconsin, United States

  • The Children's Hospital at Westmead, Westmead, New South Wales, Australia

  • Murdoch Children's Research Institute, Parkville, Victoria, Australia

  • Otto-von-Guericke Universitaet, Universitaetskinderklinik, Magdeburg, Germany

  • Universitätsklinikum Münster, Münster, Germany

  • Osaka University Hospital, Osaka, Japan

  • Saitama Children's Medical Center, Saitama, Japan

  • Tokushima University Hospital, Tokushima, Japan

  • Institut Catala de Traumatologica I Medicina de l'Esport, Barcelona, Spain

  • Hospital Sant Joan de Deu, Barcelona, Spain

  • Hospital Universitario Virgen de la Victoria, Málaga, Spain

  • Acibadem University School of Medicine, Istanbul, Turkey (Türkiye)

  • Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London, United Kingdom

  • Sheffield Children's NHS Foundation Trust, Sheffield, United Kingdom

מובילי המחקר
  • Medical Director, MD

    Study Director

    BioMarin Pharmaceutical