Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE2, PHASE3

מצבים רפואיים

Achondroplasia

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

    Contact: Study coordinator (Hind Al-Saif)
  • Nemours Children's Health, Wilmington, Delaware, United States

    Contact: Study coordinator (Mahim Jain)
  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

  • Johns Hopkins Medicine, Baltimore, Maryland, United States

    Contact: Study coordinator (Julie Hoover-Fong)
  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

    Contact: Study coordinator (Benjamin Cocanougher)
  • Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

    Contact: Study coordinator (David Weber)
  • University of Texas Southwestern Medical Center, Dallas, Texas, United States

    Contact: Study coordinator (Nadia Merchant)
  • Texas Children Hospital, Baylor College of Medicine, Houston, Texas, United States

    Contact: Study coordinator (Carlos Bacino)
  • Consano Clinical Research, LLC, San Antonio, Texas, United States

    Contact: Study coordinator (Daniel Katselnik)
  • Murdoch Children's Research Institute, Parkville, Victoria, Australia

    Contact: Study coordinator (Ravi Savarirayan)
  • Universite de Montreal - Centre Hospitalier Universitaire Sainte-Justine, Montreal, Quebec, Canada

    Contact: Study coordinator (Philippe Campeau)
  • Irccs Ospedale Gaslini Di Genova, Genova, Italy

    Contact: Study coordinator (Mohamed Maghnie)
  • Uniwersytecki Szpital Kliniczny im. J. Mikulicza-Radeckiego we Wroclawiu Klinika Pediatrii i Chorob Infekcyjnych, Wroclaw, Poland

    Contact: Study coordinator (Robert Shanislaw Smigiel)
  • Institutul National de Endocrinologie C.I.Parhon, Bucharest, Romania

    Contact: Study coordinator (Iuliana Gherlan)
  • Craiova Emergency Clinical County, Craiova, Romania

    Contact: Study coordinator (Ioana Streata)
  • Seoul National University Hospital, Seoul, South Korea

  • Pusan National University Yangsan Hospital, Yangsan, South Korea

    Contact: Study coordinator (Chong-Kun Cheon)
  • University Hospitals Bristol NHS Foundation Trust - Bristol Royal Hospital for Children, Bristol, United Kingdom

    Contact: Study coordinator (Toby Candler)
מובילי המחקר
  • Medical Director, PhD

    Study Director

    BioMarin Pharmaceutical