Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
מצבים רפואיים
Myotonic Dystrophy Type 1 (DM1) · DM1 · Myotonic Dystrophy · Steinert Disease · Steinert
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
UCSD - Altman Clinical and Translational Research Institute, La Jolla, California, United States
Rare Disease Research, LLC, Atlanta, Georgia, United States
IU Health Neuroscience Center, Indianapolis, Indiana, United States
Roy Blunt NextGen Precision Health Institute, Columbia, Missouri, United States
Rare Disease Research, LLC, Hillsborough, North Carolina, United States
The University of Texas Health Science Center at San Antonio, San Antonio, Texas, United States
Virginia Commonwealth University - Biotech One, Richmond, Virginia, United States
UZ Leuven, Leuven, Belgium
Rigshospitalet, (Neuromuscular Clinic and Research Unit, Department 8077), Copenhagen, Denmark
Contact: Study coordinator (Nicolai Rasmus Preisler) · nicolai.rasmus.preisler@regionh.dk · 45 35457257CHU de Nantes - Hôtel-Dieu, Nantes, France
Pitié-Salpêtrière Hospital, Paris, France
Contact: Study coordinator (Nassima Ait Tahar) · n.ait-tahar@institut-myologie.org · + 33 1 42 16 37 63CHU de Toulouse - Hôpital Pierre-Paul Riquet, Toulouse, France
Contact: Study coordinator (Antoine Faurie-Grépon) · antoine.faurie-grepon@inserm.fr · +33 5 61 77 91 26LMU Klinikum der Universität München Neurologische Klinik und Poliklinik Friedrich-Baur-Institut Campus Innenstadt, Munich, Bavaria, Germany
Contact: Study coordinator (Riccardo Morbio) · Riccardo.Morbio@med.uni-muenchen.de · + 49 89 4400 72523Charité Universitätsmedizin Berlin Campus-Buch Muscle Research Unit, Berlin, State of Berlin, Germany
Contact: Study coordinator (Elisabetta Gazzerro, Dr med) · Elisabetta.gazzerro@charite.de · 0049 172 23 53 192Centro Clinico Nemo Milano, Fondazione Serena ETS, Milan, Milano, Italy
Contact: Study coordinator (Erica Di Natale) · erica.dinatale@centrocliniconemo.it · +39 02 91433764National Hospital Organization Osaka Toneyama Medical Center, Toyonaka-Shi, Osaka, Japan
Contact: Study coordinator (Tsuyoshi Matsumura, MD, PhD) · matsumura.tsuyoshi.kq@mail.hosp.go.jp · 81668532001Yamaguchi University Hospital, Ube-Shi, Yamaguchi, Japan
Hospital Universitario Infanta Sofía, San Sebastián de los Reyes, Madrid, Spain
University College London Hospitals NHS Foundation Trust National Hospital for Neurology and Neurosurgery, London, England, United Kingdom