PrP-targeting siRNA Safety & Mechanism Study
Conditions
Prion Disease
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Massachusetts General Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Steven E Arnold, MD)Mayo Clinic, Rochester, Minnesota, United States
Contact: Principal Investigator (Vijay K Ramanan, MD PhD)Columbia University Medical Center, New York, New York, United States
Contact: Principal Investigator (Lawrence Honig, MD PhD)University Hospitals Cleveland Medical Center, Cleveland, Ohio, United States
Contact: Study coordinator (Mary Andrews, BA, RRT, CCRP) · mary.andrews@uhhospitals.org · 216-844-2386Contact: Principal Investigator (Brian S Appleby, MD)Vanderbilt University Medical Center, Nashville, Tennessee, United States
Contact: Principal Investigator (Amanda Peltier, MD)
Study leads
Eric V Minikel, PhD
Principal Investigator
Broad Institute of MIT and Harvard