Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
Conditions
Achondroplasia
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
Contact: Study coordinator (Hind Al-Saif)Nemours Children's Health, Wilmington, Delaware, United States
Contact: Study coordinator (Mahim Jain)Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Johns Hopkins Medicine, Baltimore, Maryland, United States
Contact: Study coordinator (Julie Hoover-Fong)Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
Contact: Study coordinator (Benjamin Cocanougher)Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Study coordinator (David Weber)University of Texas Southwestern Medical Center, Dallas, Texas, United States
Contact: Study coordinator (Nadia Merchant)Texas Children Hospital, Baylor College of Medicine, Houston, Texas, United States
Contact: Study coordinator (Carlos Bacino)Consano Clinical Research, LLC, San Antonio, Texas, United States
Contact: Study coordinator (Daniel Katselnik)Murdoch Children's Research Institute, Parkville, Victoria, Australia
Contact: Study coordinator (Ravi Savarirayan)Universite de Montreal - Centre Hospitalier Universitaire Sainte-Justine, Montreal, Quebec, Canada
Contact: Study coordinator (Philippe Campeau)Irccs Ospedale Gaslini Di Genova, Genova, Italy
Contact: Study coordinator (Mohamed Maghnie)Uniwersytecki Szpital Kliniczny im. J. Mikulicza-Radeckiego we Wroclawiu Klinika Pediatrii i Chorob Infekcyjnych, Wroclaw, Poland
Contact: Study coordinator (Robert Shanislaw Smigiel)Institutul National de Endocrinologie C.I.Parhon, Bucharest, Romania
Contact: Study coordinator (Iuliana Gherlan)Craiova Emergency Clinical County, Craiova, Romania
Contact: Study coordinator (Ioana Streata)Seoul National University Hospital, Seoul, South Korea
Pusan National University Yangsan Hospital, Yangsan, South Korea
Contact: Study coordinator (Chong-Kun Cheon)University Hospitals Bristol NHS Foundation Trust - Bristol Royal Hospital for Children, Bristol, United Kingdom
Contact: Study coordinator (Toby Candler)
Study leads
Medical Director, PhD
Study Director
BioMarin Pharmaceutical