PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Arkansas Children's Hospital, Little Rock, Arkansas, United States
Contact: Study coordinator (Kristin MacLean) · MacleanKD@archildrens.org · 501-364-2079
Contact: Principal Investigator (Aravindhan Veerapandiyan, MD)
Washington University School of Medicine, St Louis, Missouri, United States
Contact: Study coordinator (Natalie Goedeker) · NeuromusclePediatricResearch@wustl.edu · 314-362-4919
Contact: Principal Investigator (Craig Zaidman, MD)

View source on ClinicalTrials.gov