Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening

Abroad (travel likely)Recruiting

Conditions

Spinal Muscular Atrophy (SMA) · Duchenne Muscular Dystrophy (DMD)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle, Liège, Belgium
Contact: Study coordinator (Tamara Dangouloff, PhD) · tamara.dangouloff@uliege.be · 0033662438138

Study leads

Tamara Dangouloff, PhD
Principal Investigator
University of Liege
Laurent Servais, MD, PhD
Study Director
University of Liege

View source on ClinicalTrials.gov

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