A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

Abroad (travel likely)RecruitingPHASE3

Conditions

Hemophilia

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles, California, United States

  • The Center for Inherited Blood Disorders- Site Number : 8400009, Orange, California, United States

  • Cure 4 The Kids Foundation- Site Number : 8400001, Las Vegas, Nevada, United States

  • Hackensack Meridian Health - Hackensack University Medical Center- Site Number : 8400008, Hackensack, New Jersey, United States

  • University of Texas - Southwestern Medical Center- Site Number : 8400015, Dallas, Texas, United States

  • Investigational Site Number : 0560002, Brussels, Belgium

    Contact: Study coordinator (Bernard Wenderickx) · Bernard.wenderickx@hubruxelles.be · +32 2 24 77 36 54
    Contact: Principal Investigator (Phu Quoc Lê)
  • Investigational Site Number : 0560001, Brussels, Belgium

    Contact: Study coordinator (Alix Blore) · alix.blore@saintluc.uclouvain.be · +32 2 764 23 37
    Contact: Principal Investigator (An Van Damme)
  • Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 0760003, Ribeirão Preto, São Paulo, Brazil

    Contact: Study coordinator (Ana Beatriz Nicolau Perim) · +55 16 3963 6480
    Contact: Principal Investigator (Luciana Oliveira)
  • Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 0760004, São Paulo, Brazil

  • Investigational Site Number : 1240001, Hamilton, Ontario, Canada

  • Investigational Site Number : 1240003, Montreal, Quebec, Canada

  • Investigational Site Number : 1560001, Beijing, China

  • Investigational Site Number : 3560004, Bengaluru, India

  • Investigational Site Number : 3560002, Mumbai, India

  • Investigational Site Number : 3560001, Pune, India

  • Investigational Site Number : 3560003, Vellore, India

  • Investigational Site Number : 3800002, Florence, Firenze, Italy

  • Investigational Site Number : 3800001, Milan, Milano, Italy

    Contact: Study coordinator (Flora Peyvandi) · flora.peyvandi@policlinico.mi.it · +39 02 5503.5414
    Contact: Principal Investigator (Flora Peyvandi)
  • Investigational Site Number : 3800003, Rozzano, Milano, Italy

    Contact: Study coordinator (Maria Elisa Mancuso) · mariaelisa.mancuso@hunimed.eu · +39 0282245981
    Contact: Principal Investigator (Maria Elisa Mancuso)
  • Investigational Site Number : 6160002, Wroclaw, Lower Silesian Voivodeship, Poland

    Contact: Study coordinator (Marta Hetman) · martha.hetman@gmail.com · +48 530060737
    Contact: Principal Investigator (Elzbieta Latos-Grazynska)
  • Investigational Site Number : 6420001, Iași, Romania

  • Investigational Site Number : 6420003, Timișoara, Romania

  • Investigational Site Number : 6820001, Riyadh, Saudi Arabia

  • Investigational Site Number : 7240001, Esplugues de Llobregat, Barcelona [Barcelona], Spain

  • Investigational Site Number : 7240002, Madrid, Spain

  • Investigational Site Number : 7240003, Zaragoza, Spain

  • Investigational Site Number : 1580002, Taichung, Taiwan

  • Investigational Site Number : 1580001, Taipei, Taiwan

  • Investigational Site Number : 7920001, Istanbul, Turkey (Türkiye)

    Contact: Study coordinator (Funda Ciga) · +90 533 420 60 57
    Contact: Principal Investigator (Basak Koc Senol)
  • Investigational Site Number : 7920002, Izmir, Turkey (Türkiye)

    Contact: Study coordinator (Esra Nur Nalçakan Sağlam) · +90 (538) 322 67 22
    Contact: Principal Investigator (Kaan Kavakli)