A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy

Abroad (travel likely)RecruitingPHASE1

Conditions

Dilated Cardiomyopathy (DCM)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • University of California, San Diego, San Diego, California, United States

    Contact: Study coordinator (Clinical Research Coordinator) · emoyacespedes@health.ucsd.edu · 858-822-1722
    Contact: Principal Investigator (Barry Greenberg, MD)
  • Mayo Clinic, Rochester, Minnesota, United States

    Contact: Study coordinator (Clinical Research Coordinator) · slade.sierra@mayo.edu · 507-538-1500
    Contact: Principal Investigator (John Giudicessi, MD, PhD)
  • Medical University of South Carolina, Charleston, South Carolina, United States

    Contact: Study coordinator (Clinical Res) · andrewcl@musc.edu · 843-792-2300
    Contact: Principal Investigator (Daniel Judge, MD)