A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy
Conditions
Dilated Cardiomyopathy (DCM)
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
University of California, San Diego, San Diego, California, United States
Contact: Study coordinator (Clinical Research Coordinator) · emoyacespedes@health.ucsd.edu · 858-822-1722Contact: Principal Investigator (Barry Greenberg, MD)Mayo Clinic, Rochester, Minnesota, United States
Contact: Principal Investigator (John Giudicessi, MD, PhD)Medical University of South Carolina, Charleston, South Carolina, United States
Contact: Principal Investigator (Daniel Judge, MD)