Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE2

מצבים רפואיים

Pompe Disease

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • University of California - Irvine Medical Center, Irvine, California, United States

  • University of Florida (UF) - Gainesville, Gainesville, Florida, United States

  • Emory University Hospital, Atlanta, Georgia, United States

  • Washington University in St. Louis, St Louis, Missouri, United States

  • Duke University Medical Center, Durham, North Carolina, United States

  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

  • University of Pennsylvania, Philadelphia, Pennsylvania, United States

  • University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States

  • Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax, Virginia, United States

  • UZ Leuven, Leuven, Belgium

  • Aarhus University Hospital, Aarhus, Denmark

  • HLC Hopital Pierre Wertheimer, Bron, France

  • AP-HP Hopital Raymond Poincare, Garches, France

  • Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille, France

  • CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice, France

  • Universitaetsklinikum Halle (Saale), Halle, Germany

  • SphinCS GmbH, Höchheim, Germany

  • Klinikum der Ludwig-Maximilians-Universitaet Muenchen, München, Germany

  • A.O.U. Policlinico "G. Martino", Messina, Italy

  • AOU Citta della Salute e della Scienza di Torino - Ospedale le Molinette, Torino, Italy

  • Erasmus MC, GE Rotterdam, GE Rotterdam, Netherlands

  • Hospital Universitario 12 de Octubre, Madrid, Spain

  • Hospital Universitari i Politecnic La Fe, Valencia, Spain

  • Queen Elizabeth Hospital Birmingham, Birmingham, United Kingdom

  • National Hospital for Neurology & Neurosurgery, London, United Kingdom

  • Royal Free London NHS Foundation Trust, London, United Kingdom

  • Royal Victoria Infirmary, Newcastle upon Tyne, United Kingdom

  • Salford Royal Hospital, Salford, United Kingdom