Pharmacokinetics, Efficacy, and Safety of Encaleret in Pediatric Participants With Autosomal Dominant Hypocalcemia Type 1 (ADH1)

Abroad (travel likely)RecruitingPHASE2, PHASE3

Conditions

Autosomal Dominant Hypocalcemia Type 1 (ADH1)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Yale University, New Haven, Connecticut, United States

  • Children's National Medical Center, Washington D.C., District of Columbia, United States

  • Nemours Children's Health, Jacksonville, Florida, United States

  • The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

  • Royal London Hospital, London, United Kingdom

  • Royal Manchester Children's Hospital, Manchester, United Kingdom

Study leads
  • Calcilytix Medical Director

    Study Director

    Calcilytix Therapeutics, Inc., a BridgeBio company