חזרה לתוצאות החיפוש

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE3

מצבים רפואיים

Niemann-Pick Type C Disease · GM1 Gangliosidosis · GM2 Gangliosidosis

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים

  • UCSF Children's Hospital and Research Center at Oakland, Oakland, California, United States

    Contact: Study coordinator (Veronica Cheung, CRC) · Veronica.Cheung@ucsf.edu · 510-428-3885
    Contact: Principal Investigator (Caroline Hastings, MD)

  • University of Minnesota Medical School, Minneapolis, Minnesota, United States

  • Mayo Clinic Childrens Center - PIN, Rochester, Minnesota, United States

  • Children's Medical Center Dallas, Dallas, Texas, United States

  • Lysosomal Rare Disorders Research and Treatment Center, Fairfax, Virginia, United States

    Contact: Study coordinator (Lauren Noll) · lnoll@ldrtc.org · 571-732-4655

  • Hospital Universitario Austral, Ciudad Autónoma Buenos Aires, Buenos Aires, Argentina

  • Hospital de Niños de La Santisima Trinidad, Córdoba, Córdoba Province, Argentina

  • Women's and Children's Hospital, North Adelaide, South Australia, Australia

    Contact: Study coordinator (Louise Jaensch) · louise.jaensch@sa.gov.au · +61 881 616 610

  • Royal Melbourne Hospital, Parkville, Victoria, Australia

    Contact: Study coordinator (Karen Chidgey) · NeuropsychiatryResearch@mh.org.au

  • Royal Children's Hospital Melbourne - PIN, Parkville, Victoria, Australia

    Contact: Study coordinator (Heidi Peters) · metabolictrials@mcri.edu.au · +61 03 9345 6205

  • Instituto Fernandes Figueira, Rio de Janeiro, Rio de Janeiro, Brazil

    Contact: Study coordinator (DAFNE D. G. HOROVITZ) · dafne.horovitz@fiocruz.br · +55 21 2554-1709

  • Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre, Rio Grande do Sul, Brazil

    Contact: Study coordinator (Paula de Castro Pereira) · paulapereira@hcpa.edu.br · +55 513 359 6340
    Contact: Principal Investigator (Roberto Giugliani)

  • Hospital Pequeno Príncipe, Curitiba, Brazil

    Contact: Study coordinator (Daniel Almeida do Valle) · daniel.valle@hpp.org.br · +55 41 9825-0325

  • M.A.G.I.C. Clinic Ltd. Metabolics and Genetics in Calgary, Calgary, Alberta, Canada

  • University of Alberta Medical Genetics Clinic, Edmonton, Alberta, Canada

    Contact: Study coordinator (Casey Brodie) · casey.brodey@albertahealthservices.ca · +1 780-492-9277

  • Centre Hospitalier de l'Universite de Montreal-1000 rue Saint-Denis, Montreal, Quebec, Canada

  • AP-HP - Hôpital Armand Trousseau, Paris, France

    Contact: Study coordinator (Aurelie Phelep) · a.phelep@institut-myologie.org · +33 01-71-73-82-16

  • SphinCS GmbH, Höchheim, Germany

  • Amrita Institute of Medical Sciences and Research Centre, Ernākulam, Kerala, India

    Contact: Study coordinator (Sheela Nampoothiri) · sheelanampoothiri@aims.amrita.edu · +91 9447978222

  • All India Institute of Medical Sciences (AIIMS) - New Delhi, New Delhi, National Capital Territory of Delhi, India

    Contact: Study coordinator (Faijan Beg) · faijan.crds@outlook.com · +91 78283 96432

  • JK Lone Hospital, Jaipur, Rajasthan, India

    Contact: Study coordinator (Priyanshu Mathur) · Priyanshujkl@gmail.com · +91 9982451490

  • Christian Medical College and Hospital, Vellore, Tamil Nadu, India

  • Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy

    Contact: Study coordinator (Anna Ardissone) · anna.ardissone@istituto-besta.it · +39 0223942210

  • Hospital Universitario Dr. Jose Eleuterio González, Monterrey, Nuevo León, Mexico

  • Centenario Hospital Miguel Hidalgo, Aguascalientes, Mexico

  • The Children's Hospital & the University of Child Health Lahore, Lahore, Punjab Province, Pakistan

  • ULS de Santo António, EPE - Centro Materno Infantil Norte, Porto, Porto District, Portugal

    Contact: Study coordinator (Anabela Bandeira) · anabelabandeira.dca@chporto.min-saude.pt · +35 915676520

  • ULS de Santa Maria,EPE - Hospital de Santa Maria - PPDS, Lisbon, Portugal

    Contact: Study coordinator (Tiago Proenca dos Santos) · cic@ulssm.min.saude.pt · +351 210405814

  • Hospital Universitario Vall d'Hebron - PPDS, Barcelona, Barcelona, Spain

    Contact: Study coordinator (Nuria Leal) · nuria.leal@vhir.org · +34677171367

  • Hospital Infantil Universitario Niño Jesus - PIN, Madrid, Madrid, Spain

    Contact: Study coordinator (Beatriz Bernardino Cuesta) · neurologia.hnjs@salud.madrid.org

  • Sahlgrenska universitetssjukhuset Östra, Gothenburg, Västra Götaland County, Sweden

    Contact: Study coordinator (Niklas Darin) · niklas.darin@vgregim.se · 0046 31 3438213

  • Inselspital - Universitätsspital Bern, Bern, Canton of Bern, Switzerland

    Contact: Study coordinator (Sandrina Schneider) · sandrina.schneider@insel.ch · +41 31 63 2 07 41

  • Balcali Hastanesi Saglik Uygulama ve Arastirma Merkezi, Adana, Adana, Turkey (Türkiye)

  • Gazi Universitesi Saglik Arastirma ve Uygulama Merkezi, Çankaya, Ankara, Turkey (Türkiye)

  • Ege Universitesi Tip Fakultesi, Bornova, İzmir, Turkey (Türkiye)

  • Great Ormond Street Hospital, London, London, United Kingdom

  • University College London Hospitals (UCLH), London, Middlesex, United Kingdom

  • Royal Manchester Children's Hospital, Manchester, United Kingdom

צפייה במקור ב־ClinicalTrials.gov(נפתח בחלון חדש)