A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety

Abroad (travel likely)RecruitingPHASE3

Conditions

Epileptic Encephalopathy · SCN2A Encephalopathy

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Praxis Research Site, San Diego, California, United States

  • Praxis Research Site, Aurora, Colorado, United States

  • Praxis Research Site, Chicago, Illinois, United States

  • Praxis Research Site, Cincinnati, Ohio, United States

  • Praxis Research Site, Philadelphia, Pennsylvania, United States

  • Praxis Research Site, Memphis, Tennessee, United States

  • Praxis Research Site, Porto Alegre, Brazil

  • Praxis Research Site, São Paulo, Brazil

  • Praxis Research Site, Bonn, Bonn, Germany

  • Praxis Research Site, Rome, Italy

Study leads
  • Medical Director

    Study Director

    Praxis Precision Medicines